Acts of Friendship. For Ashley, it was like this: She was sitting with a big group in the school lunchroom when she accidentally knocked her drink onto her lap. As word spread that it looked like Ashley had wet herself, the laughter began to mount. Then she noticed her best friend doing something strange.
The price â listed as $23,800 for a 28-day supply â is slightly higher than the $300,000 average annual cost of Genzymeâs flagship Gaucher treatment Cerezyme, a protein-based enzyme replacement therapy that patients typically take by two-hour infusions every two weeks. Advertisement.
Limiting certain substances in the diet can help prevent the buildup of potentially toxic substances that are normally broken down by the enzyme. In some cases, enzyme replacement therapy can help compensate for the enzyme shortage. These treatments are used to manage existing signs and symptoms and may help prevent future complications. For other genetic conditions, treatment and management strategies are designed to improve particular signs and symptoms associated with the disorder.