stat.AP
Challenges and Possible Strategies to Address Them in Rare Disease Drug Development: A Statistical Perspective
Jie Chen Lei Nie Shiowjen Lee Haitao Chu Haijun Tian Yan Wang Weili He Thomas Jemielita Susan Gruber Yang Song Roy Tamura Lu Tian Yihua Zhao Yong Chen Mark van der Laan Hana Lee