Discussion
TSC
In this study, we demonstrated the effectiveness and safety aspects of treatment with everolimus in 64 patients with TSC in Norway and Denmark. This is one of few unselected, population-based studies from clinical practice in countries with similar health care systems, characterised by high-quality follow-up and equal access to health care. In the following sections, we compare the outcome measures with results from the randomised, double-blinded, placebo-controlled EXIST studies [