Study participants
nonmalignant disease
PID, OBESE, HBP
Pediatric patients 28 days to less than 18 years of age with nonmalignant disease including IEM, PID, HBP, and BMF were eligible. Only patients with an indication for a first allogeneic HSCTs were enrolled if a matched sibling donor, matched family donor, matched unrelated donor, or umbilical cord blood was available. Lansky Performance Scores or Karnofsky Performance Scores for those ≥16 years of age had to be at least 70%. Main exclusion criteria included obese pediatric patients with body mass index > 30 kg/m