Outcomes
death, TTP, malignant disease
TTP, MALIGNANT DISEASE
As of August 2019, a total of 4 (10%) patients were alive and on follow-up. The median follow-up was 3.2 years. The cause of death was attributed to malignant disease in 18 participants (50%), to other causes in 3 patients (8.3%), and unknown in 15 (42%) patients.The response rate (RR) for complete response (CR) or partial response (PR) (CR + PR) was 72.5% (Primary objectives.Median TTP was 10.78 months (95% CI, 263-525) (