Supplementary Information
SPINAL MUSCULAR ATROPHY 1
Below is the link to the electronic supplementary material.Supplementary file1 (DOCX 49 kb)The authors would like to thank all individuals enrolled in the risdiplam studies, their families, and the site staff involved. The authors would also like to thank the Spinal Muscular Atrophy Foundation and PTC Therapeutics for their collaboration in the SUNFISH study. Jen Ciarochi of Nucleus Global, wrote the first draft of the manuscript based on an outline agreed by all authors and provided medical writing assistance with subsequent drafts in accordance with Good Publication Practice (GPP3) guidelines (