A baby with his mum and a nurse who are discussing

Innovating in rare diseases


Innovating in rare diseases

Life is a health journey that for some starts with being born with a rare genetic disorder. There are more than 7,000 rare diseases in the world, and 30% of children affected die before reaching their 5th birthday.

A baby in his grand-parents’ arms

As a health journey partner,

Sanofi has been working on several rare diseases, including for example enzyme replacement therapy to treat Gaucher disease, considered an ultra-rare disease with fewer than 10,000 patients globally.